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Top 10 search results for "Clinical trials" in Resources. To see all results and access other features, sign up for free.

Clinical trials are designed with safety as a primary concern.Before a new drug, new dosage, or n...
Are Clinical Trials Safe for People With SMA?
Clinical trials are designed with safety as a primary concern.Before a new drug, new dosage, or n...
Clinical trials for spinal muscular atrophy (SMA) test new treatments, new dosages of existing tr...
How Do Clinical Trials Work for SMA?
Clinical trials for spinal muscular atrophy (SMA) test new treatments, new dosages of existing tr...
Clinical trials may test new drugs or new dosages or combinations of drugs for spinal muscular at...
5 Reasons To Consider Participating in SMA Clinical Trials
Clinical trials may test new drugs or new dosages or combinations of drugs for spinal muscular at...
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Spinal muscular atrophy (SMA) mainly affects children, but adults can have it, too — about 35 per...
SMA Treatment for Children vs. Adults: 5 Key Differences
Spinal muscular atrophy (SMA) mainly affects children, but adults can have it, too — about 35 per...
Researchers are studying a potential new treatment called taldefgrobep alfa for spinal muscular a...
Posted 08/17/2022
Study Recruiting for New Add-On SMA Treatment
Researchers are studying a potential new treatment called taldefgrobep alfa for spinal muscular a...
Posted 08/17/2022
Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022
New Study: Zolgensma May Benefit Adults With SMA Types 2 and 3
Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022
The University of Rochester Center for Health + Technology is seeking caregivers of children with...
Posted 09/15/2021
Caregivers Sought for SMA Outcome Tool Validation Study
The University of Rochester Center for Health + Technology is seeking caregivers of children with...
Posted 09/15/2021