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Study Recruiting for New Add-On SMA Treatment
Researchers are studying a potential new treatment called taldefgrobep alfa for spinal muscular a...
Posted 08/17/2022
Study Recruiting for New Add-On SMA Treatment
Researchers are studying a potential new treatment called taldefgrobep alfa for spinal muscular a...
Posted 08/17/2022
Causes of Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is a genetic neuromuscular disorder characterized by muscle weaknes...
Causes of Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is a genetic neuromuscular disorder characterized by muscle weaknes...
Scoliosis Surgery in Kids With SMA Can Cause Serious Complications, Research Finds
Corrective surgery for scoliosis in children with spinal muscular atrophy (SMA) type 1 can lead t...
Posted 01/18/2022
Scoliosis Surgery in Kids With SMA Can Cause Serious Complications, Research Finds
Corrective surgery for scoliosis in children with spinal muscular atrophy (SMA) type 1 can lead t...
Posted 01/18/2022
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Can You Walk With Spinal Muscular Atrophy? 4 Things To Know
If your child was recently diagnosed with spinal muscular atrophy (SMA) — or if you were recently...
Can You Walk With Spinal Muscular Atrophy? 4 Things To Know
If your child was recently diagnosed with spinal muscular atrophy (SMA) — or if you were recently...
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
What Is Finkel Type SMA?
Finkel type SMA (SMAFK) is a rare type of adult-onset (or late-onset) spinal muscular atrophy (SM...
What Is Finkel Type SMA?
Finkel type SMA (SMAFK) is a rare type of adult-onset (or late-onset) spinal muscular atrophy (SM...
SMA and Congenital Myasthenic Syndrome: What's the Difference?
Congenital myasthenic syndrome (CMS) refers to a group of disorders that cause muscle weakness, o...
SMA and Congenital Myasthenic Syndrome: What's the Difference?
Congenital myasthenic syndrome (CMS) refers to a group of disorders that cause muscle weakness, o...
New Study: Zolgensma May Benefit Adults With SMA Types 2 and 3
Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022
New Study: Zolgensma May Benefit Adults With SMA Types 2 and 3
Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022