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Top 10 search results for "Zolgensma" in Resources. To see all results and access other features, sign up for free.

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SMA Medication Zolgensma May Cause Liver Failure, Warns New Label Update
Zolgensma (onasemnogene abeparvovec-xioi), a treatment for children with spinal muscular atrophy ...
Posted 11/30/2021
SMA Medication Zolgensma May Cause Liver Failure, Warns New Label Update
Zolgensma (onasemnogene abeparvovec-xioi), a treatment for children with spinal muscular atrophy ...
Posted 11/30/2021
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
Spinraza Alone May Be Better Than Combining It With Zolgensma To Treat SMA Type 1
A recent study has found that combining Zolgensma and Spinraza does not improve motor or respirat...
Posted 02/23/2022
Spinraza Alone May Be Better Than Combining It With Zolgensma To Treat SMA Type 1
A recent study has found that combining Zolgensma and Spinraza does not improve motor or respirat...
Posted 02/23/2022
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
New Study: Zolgensma May Benefit Adults With SMA Types 2 and 3
Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022
New Study: Zolgensma May Benefit Adults With SMA Types 2 and 3
Zolgensma, a formulation of onasemnogene abeparvovec-xioi, is a type of gene therapy that can hel...
Posted 11/16/2022
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
SMA Treatment for Children vs. Adults: 5 Key Differences
Spinal muscular atrophy (SMA) mainly affects children, but adults can have it, too — about 35 per...
SMA Treatment for Children vs. Adults: 5 Key Differences
Spinal muscular atrophy (SMA) mainly affects children, but adults can have it, too — about 35 per...
Spinal Muscular Atrophy Type 1
Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...
Spinal Muscular Atrophy Type 1
Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...
Can You Walk With Spinal Muscular Atrophy? 4 Things To Know
If your child was recently diagnosed with spinal muscular atrophy (SMA) — or if you were recently...
Can You Walk With Spinal Muscular Atrophy? 4 Things To Know
If your child was recently diagnosed with spinal muscular atrophy (SMA) — or if you were recently...
Bone Fractures and Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is caused by a mutation of the survival motor neuron 1 (SMN1) gene....
Bone Fractures and Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is caused by a mutation of the survival motor neuron 1 (SMN1) gene....