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Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
How To Appeal an Insurance Company Denial for SMA
If you are living with spinal muscular atrophy (SMA), you’re likely aware of the high costs assoc...
How To Appeal an Insurance Company Denial for SMA
If you are living with spinal muscular atrophy (SMA), you’re likely aware of the high costs assoc...
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
The Importance of Splicing in SMA Treatment
Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...
The Importance of Splicing in SMA Treatment
Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...
Risdiplam Safe and Effective After 24 Months of Treatment in Babies With Type 1 SMA
In a recently published study, 41 infants with type 1 spinal muscular atrophy (SMA) were treated...
Posted 08/27/2021
Risdiplam Safe and Effective After 24 Months of Treatment in Babies With Type 1 SMA
In a recently published study, 41 infants with type 1 spinal muscular atrophy (SMA) were treated...
Posted 08/27/2021
New Trial Will Test Higher Dose of Nusinersen for People With Later-Onset SMA
A new clinical trial will study whether a higher dose of nusinersen will help people with spinal ...
Posted 10/05/2021
New Trial Will Test Higher Dose of Nusinersen for People With Later-Onset SMA
A new clinical trial will study whether a higher dose of nusinersen will help people with spinal ...
Posted 10/05/2021
Spinal Muscular Atrophy Treatment and Therapy Options
Until recently, treatments for spinal muscular atrophy (SMA) could manage only symptoms. Doctors ...
Spinal Muscular Atrophy Treatment and Therapy Options
Until recently, treatments for spinal muscular atrophy (SMA) could manage only symptoms. Doctors ...