Clinical trials

Overview
Depending on several factors, you may be eligible to participate in clinical trials studying new treatments for spinal muscular atrophy (SMA). Eligibility may be based on specifics of your or your child’s… read more

Evrysdi (Risdiplam)

Overview
Evrysdi is a prescription medication approved by the U.S. Food and Drug Administration (FDA) to treat children and adults with spinal muscular atrophy (SMA). Evrysdi is also known by its drug name, risdiplam.

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Exercise

Overview
Exercise can help most people stay healthy and feel their best. Exercise can reduce stress, lower blood pressure and cholesterol, improve sleep, promote a healthy weight, and help prevent the development of… read more

Gastrostomy tube (G-tube)

Overview
The gastrostomy tube (G-tube) is a flexible feeding tube surgically inserted through the abdominal wall and directly into the stomach. It bypasses the mouth and esophagus, delivering food, liquid, and… read more

Immunizations

Overview
Children or adults with SMA are at greater risk for pulmonary infection or difficulty breathing or clearing the lungs.¹ Therefore, people with SMA are at greater risk for serious complications and infections… read more

Invasive breathing support

Overview
If noninvasive ventilation (NIV) does not provide enough respiratory support, people with respiratory issues due to spinal muscular atrophy (SMA) may need greater assistance breathing.

With invasive… read more

Itvisma (Onasemnogene Abeparvovec-Brve)

Overview
Itvisma is approved by the U.S. Food and Drug Administration (FDA) for the treatment of spinal muscular atrophy (SMA) in adults and children 2 years of age and older who have a confirmed mutation (variation) in…