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Spinal Muscular Atrophy Treatment and Therapy Options
Until recently, treatments for spinal muscular atrophy (SMA) could manage only symptoms. Doctors ...
Spinal Muscular Atrophy Treatment and Therapy Options
Until recently, treatments for spinal muscular atrophy (SMA) could manage only symptoms. Doctors ...
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
The Importance of Splicing in SMA Treatment
Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...
The Importance of Splicing in SMA Treatment
Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...
Spinal Muscular Atrophy Type 1
Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...
Spinal Muscular Atrophy Type 1
Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
Causes of Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is a genetic neuromuscular disorder characterized by muscle weaknes...
Causes of Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is a genetic neuromuscular disorder characterized by muscle weaknes...