Connect with others who understand.

Sign up Log in
Quick Links
Q&A Treatments A-Z Help Center Guidelines Crisis Accessibility
Resources
Community Diagnosis & Information Managing Your Condition Treating SMA News Videos All Resources
About mySMAteam
What is This Site Terms of Use Privacy policy
Powered By

Top 10 search results for "long term data children with type 1 sma keep gaining motor skills after 3 years on evrysdi" in Resources. To see all results and access other features, sign up for free.

Posts
Resources
Q&A
People
Groups
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
Interview: Dr. Strober on Combination Therapy for Babies With SMA
Many parents of children with spinal muscular atrophy (SMA) have questions about combination ther...
Posted 09/21/2021
SMA and ALS: 5 Differences and 3 Similarities
If you or a loved one is living with spinal muscular atrophy (SMA), you may be researching to lea...
SMA and ALS: 5 Differences and 3 Similarities
If you or a loved one is living with spinal muscular atrophy (SMA), you may be researching to lea...
What Is the CHOP INTEND Motor Test for SMA?
For parents and caregivers of children with spinal muscular atrophy (SMA), every milestone is mom...
What Is the CHOP INTEND Motor Test for SMA?
For parents and caregivers of children with spinal muscular atrophy (SMA), every milestone is mom...
Spinal Muscular Atrophy Treatment and Therapy Options
Until recently, treatments for spinal muscular atrophy (SMA) could manage only symptoms. Doctors ...
Spinal Muscular Atrophy Treatment and Therapy Options
Until recently, treatments for spinal muscular atrophy (SMA) could manage only symptoms. Doctors ...
Types of Spinal Muscular Atrophy (SMA)
Spinal muscular atrophy (SMA) is an inherited neuromuscular disorder — meaning it affects the ner...
Types of Spinal Muscular Atrophy (SMA)
Spinal muscular atrophy (SMA) is an inherited neuromuscular disorder — meaning it affects the ner...
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
What Is Kugelberg-Welander Disease?
Imagine a condition that gradually weakens the muscles you rely on every day to walk, run, and li...
What Is Kugelberg-Welander Disease?
Imagine a condition that gradually weakens the muscles you rely on every day to walk, run, and li...