Connect with others who understand.

Sign up Log in
Quick Links
Q&A Treatments A-Z Help Center Guidelines Crisis Accessibility
Resources
Community Diagnosis & Information Managing Your Condition Treating SMA News Videos All Resources
About mySMAteam
What is This Site Terms of Use Privacy policy
Powered By

Top 10 search results for "evrysdi development team wins drug discovery award for oral sma treatment" in Resources. To see all results and access other features, sign up for free.

Posts
Resources
Q&A
People
Groups
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
Evrysdi Development Team Wins Drug Discovery Award for Oral SMA Treatment
The researchers who discovered and developed the spinal muscular atrophy (SMA) treatment Evrysdi...
Posted 03/09/2022
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
What Is Spinal Muscular Atrophy (SMA)?
Spinal muscular atrophy (SMA) is a rare genetic disorder that causes progressive muscle weakness ...
What Is Kugelberg-Welander Disease?
Imagine a condition that gradually weakens the muscles you rely on every day to walk, run, and li...
What Is Kugelberg-Welander Disease?
Imagine a condition that gradually weakens the muscles you rely on every day to walk, run, and li...
The Importance of Splicing in SMA Treatment
Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...
The Importance of Splicing in SMA Treatment
Spinal muscular atrophy (SMA) is a genetic disease that destroys nerve cells in the spinal cord a...
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Long-Term Data: Children With Type 1 SMA Keep Gaining Motor Skills After 3 Years on Evrysdi
New data shows that risdiplam (sold as Evrysdi) helps most infants with spinal muscular atrophy (...
Posted 06/15/2022
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
Understanding How SMA Gene Therapy Works
When a child is born with spinal muscular atrophy (SMA), a rare neuromuscular disorder, it’s the ...
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
Treatment With Evrysdi After Zolgensma Shows Benefit for SMA Type 1
Researchers reviewed four cases in which children with spinal muscular atrophy (SMA) type 1 recei...
Posted 09/02/2021
Spinal Muscular Atrophy Type 2
Spinal muscular atrophy (SMA) type 2 is a genetic condition that causes muscle weakness (hypotoni...
Spinal Muscular Atrophy Type 2
Spinal muscular atrophy (SMA) type 2 is a genetic condition that causes muscle weakness (hypotoni...
Spinal Muscular Atrophy Type 1
Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...
Spinal Muscular Atrophy Type 1
Spinal muscular atrophy (SMA) type 1 is the most common type of spinal muscular atrophy. SMA is a...
5 Reasons To Consider Participating in SMA Clinical Trials
Clinical trials may test new drugs or new dosages or combinations of drugs for spinal muscular at...
5 Reasons To Consider Participating in SMA Clinical Trials
Clinical trials may test new drugs or new dosages or combinations of drugs for spinal muscular at...