Can someone of this group tell me something about myostatin inhibitors for people with SMA?
How common or likely is it for people with SMA to die from aspirating?
I think it's best to ask your neurologist.
There was an article last November saying Zolgensma could be helpful for adults. Will they be doing a clinical trial on that soon? I have not seen anything further on it.
Wow, this is the first I've read of this. Can anybody confirm?
Yes, at 8 months old. His legs started moving in 2 days. He can now swallow, stand independently, walk short distances, and started riding a bike with training wheels. My general answer is to reply⦠read more